Media Library

Scientists in the fermentation hub of Banting 1.

Scientist in a laboratory of Banting 1, office space in the background.

Understanding spinal muscular atrophy, a rare, neuromuscular genetic disease.

Modified viruses – including adeno-associated viruses – are an efficient way to transport therapeutic genetic material to affected cells.

Early signs of spinal muscular atrophy can be subtle, and often go unseen by clinicians – which is why newborn screening is critical to help obtain a prompt diagnosis.

Manufacturing of gene therapy is complex. Novartis has developed a reproducible manufacturing process.

Novartis Gene Therapies is the world leader in gene therapy, and is reimagining medicine to transform the lives of patients.

A new, state-of-the-art gene therapy manufacturing facility in North Carolina, USA

Gene therapy – an innovative approach to treating rare, genetic diseases.

Chief Strategy & Growth Officer since July 18, 2022

Crizanlizumab clinical setting from international managed access program (MAP) infographic

President, Development and Chief Medical Officer since May 16, 2022