Sickle cell disease disproportionately affects babies in Africa, but many go undiagnosed due to lack of screening. Newborn screening is needed to save lives and improve care.

Inspired by Emily Whitehead, along with other early patients treated with CAR-T cell therapy, Novartis embarked on a pioneering journey to reimagine cancer treatment. After 10 years, we continue to relentlessly pursue new science around cell and gene therapies to transform the lives of patients today and in the future.

Caring for a baby with retinopathy of prematurity (ROP) has never been easy. But mother and social visionary Silke Mader has made it her life’s work to ensure that parents dealing with ROP and other complications today get more support than she did.

To raise awareness of the sudden and profound impact of meningococcal disease on families across the globe, world-renowned photographer Anne Geddes has joined forces with the Confederation of Meningitis Organizations (CoMO) and Novartis Vaccines and Diagnostics for the Protecting Our Tomorrows: Portraits of Meningococcal Disease project.

Raising a child with a rare disease can feel overwhelming and isolating, but many parents end up being extremely proud of their children’s achievements.

After a diagnosis of childhood cancer, Ryan faced the diagnosis and treatment of leukemia head- on with the support of his family and community.

Parents and doctors can help children understand rare diseases like TSC and SJIA with the help of cartoon dogs and comic book superheroes.

In Guatemala, social worker Eduardo Canuz fights logistical and cultural challenges while preventing women and infants from inhaling smoke.

Pneumonia causes around 2 million child deaths per year globally and the burden is especially heavy in a country like Bangladesh, where a third of the population is aged 14 or below.

Most people have never heard of spinal muscular atrophy (SMA), a rare genetic disease that affects approximately 1 in 6,000 babies born worldwide each year. Innovative research may produce treatments for patients suffering from SMA and other rare diseases.