Last Update: Oct 23, 2024
A Phase III, Randomized, Double-blind Study of Ianalumab (VAY736) Versus Placebo in Addition to First-line Corticosteroids in Primary Immune Thrombocytopenia (VAYHIT1)
ClinicalTrials.gov Identifier:
Novartis Reference Number:CVAY736I12301
All compounds are either investigational or being studied for (a) new use(s). Efficacy and safety have not been established. There is no guarantee that they will become commercially available for the use(s) under investigation.

Study Description

The purpose of this study is to evaluate the effect of two different doses of ianalumab
versus placebo in addition to first-line corticosteroids in maintaining platelet count
≥30 G/L in adult participants with primary ITP. This is a multi-center, randomized, double-blind Phase 3 study to assess the efficacy and
safety of two different doses of ianalumab compared to placebo in adults with primary ITP
(platelets count <30 G/L) who require first-line standard-of-care corticosteroids.

After completion of the screening period, the participants will enter the randomized
treatment period (ianalumab/placebo with standard of care corticosteroids).

After the treatment period, all participants will enter the follow-up period to be
monitored for efficacy and safety or safety only depending on how they respond to the
study treatment.

Primary Immune Thrombocytopenia (ITP)
Phase3
Recruiting
225
Mar 06, 2023
Dec 18, 2028
All
18 Years - (Adult, Older Adult)

Interventions

Drug

Corticosteroids

Oral or parental (if clinically justified)
Biological

Ianalumab

Intravenous infusion, prepared from concentrate solution
Drug

Placebo

Intravenous infusion, prepared from matching placebo

Eligibility Criteria

Inclusion Criteria:

- Signed informed consent prior to participation in the study.

- Male or female participants aged 18 years and older on the day of signing informed
consent

- Primary ITP diagnosed within 3 months before initiating first-line ITP therapy
(corticosteroids, IVIG)

- Platelet count below 30 G/L before starting any first-line ITP therapy
(corticosteroids, IVIG)

- Response (platelet count >=50 G/L) to corticosteroids (+/- IVIG) at any time prior
to randomization. Note: Platelet count measured within 7 days of platelet
transfusion will not be considered as response.

Key Exclusion Criteria:

- Evans syndrome or any other cytopenia (patients with anemia related to bleeding or
iron deficiency are eligible)

- Current life-threatening bleeding

- Previous ITP treatment, including splenectomy, except for corticosteroids and/or
IVIG initiated as first-line therapy for up to 28 days before randomization and
rescue corticosteroids and/or IVIG given prior to confirmed diagnosis of primary ITP
.

- Prior use of B-cell depleting therapy (e.g., rituximab).

- Absolute neutrophil count below 1.0 G/L at randomization

- Participants with concurrent coagulation disorders and/or receiving anti-platelet or
anticoagulant medication with an exemption of low dose of acetylsalicylic acid

Other protocol-defined Inclusion/Exclusion may apply.

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Caba,Buenos Aires,C1280aeb,Argentina

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Caba,Buenos Aires,C1414drk,Argentina

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Ciudad Autonoma de Bs As,Buenos Aires,C1015abo,Argentina

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Tucuman,San Miguel De Tucuman,4000,Argentina

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Buenos aires,C1039aac,Argentina

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Cordoba,5000,Argentina

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Canberra,Australian Capital Territory,2605,Australia

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Wooloongabba,Queensland,4102,Australia

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Clayton,Victoria,3168,Australia

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Melbourne,Victoria,3004,Australia

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Wien,1140,Austria

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Innsbruck,Tyrol,6020,Austria

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Salzburg,5020,Austria

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Brasschaat,2930,Belgium

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Brugge,8000,Belgium

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Leuven,3000,Belgium

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Roeselare,8800,Belgium

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Sofia,1413,Bulgaria

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Sofia,1431,Bulgaria

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Varna,9010,Bulgaria

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Plovdiv,4002,Bulgaria

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Nanchang,Jiangxi,330006,China

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Shenzhen,Guangdong,518037,China

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Bengbu,233004,China

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Xian,Shaanxi,710004,China

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Luoyang,Henan,471003,China

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Dalian,116000,China

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Taiyuan,Shanxi,030001,China

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Zhengzhou,Henan,450052,China

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Jinan,250012,China

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Chengdu,Sichuan,610041,China

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Wuhan,Hubei,430022,China

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Shijiazhuang,050000,China

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Beijing,Beijing,100044,China

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Kunming,Yunnan,650101,China

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Changsha,Hunan,410008,China

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Tianjin,300020,China

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Chongqing,Chongqing,400010,China

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Hangzhou,Zhejiang,310003,China

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Changzhou,Jiangsu,213004,China

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Guangzhou,Guangdong,510515,China

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Hangzhou,Zhejiang,310006,China

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Brno Bohunice,625 00,Czechia

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Praha 10,100 34,Czechia

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Praha,12808,Czechia

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Ostrava,Poruba,708 52,Czechia

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Paris,75014,France

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Rennes,35043,France

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Caen,14033,France

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Chambery cedex,73011,France

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Le Mans,72000,France

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Lille,59037,France

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Greifswald,17475,Germany

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Hannover,30161,Germany

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Jena,07740,Germany

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Dresden,01307,Germany

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Essen,45147,Germany

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Frankfurt,60590,Germany

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Giessen,35392,Germany

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New Territories,Hong Kong

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Debrecen,4032,Hungary

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Budapest,H-1083,Hungary

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Ahmedabad,Gujarat,380013,India

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Mumbai,Maharashtra,400012,India

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Kolkata,West Bengal,700094,India

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Trieste,TS,34129,Italy

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Vicenza,VI,36100,Italy

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Bologna,BO,40138,Italy

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Firenze,FI,50134,Italy

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Roma,RM,00168,Italy

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Sapporo,Hokkaido,060-8604,Japan

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Matsumoto-city,Nagano,399-8701,Japan

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Okayama city,Okayama,701-1192,Japan

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Osaka-city,Osaka,543-8555,Japan

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Nagakute-city,Aichi,480-1195,Japan

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Iruma-gun,Saitama,350-0495,Japan

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Gifu shi,Gifu,500 8513,Japan

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Chiba,260-0852,Japan

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Shibukawa-city,Gunma,377-0280,Japan

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Fukuoka,815-8555,Japan

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Kuching,Sarawak,93586,Malaysia

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Johor Bahru,80100,Malaysia

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Kuala Lumpur,56000,Malaysia

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Penang,10050,Malaysia

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Selangor,68000,Malaysia

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Morelia,Michoacan,58260,Mexico

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Monterrey,Nuevo Leon,64460,Mexico

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Ciudad De Mexico,Mexico CP,14080,Mexico

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Gralum,1714,Norway

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Bucharest,District 2,022328,Romania

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Bucharest,030171,Romania

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Bucuresti,013975,Romania

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Madrid,28046,Spain

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Murcia,30008,Spain

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Sevilla,Andalucia,41013,Spain

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Salamanca,Castilla Y Leon,37007,Spain

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Barcelona,Catalunya,08035,Spain

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Madrid,28009,Spain

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Bangkok,10330,Thailand

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Bangkok,10700,Thailand

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Chiang Mai,50200,Thailand

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Aydin,09100,Turkey

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Edirne,22030,Turkey

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Istanbul,34214,Turkey

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Izmir,35100,Turkey

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Samsun,55139,Turkey

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Istanbul,TUR,34098,Turkey

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Southampton,So16 6yd,United Kingdom

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Glasgow,G31 2er,United Kingdom

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Leeds,Ls1 3ex,United Kingdom

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Liverpool,L7 8xp,United Kingdom

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London,Sw17 0qt,United Kingdom

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London,W12 0hs,United Kingdom

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Truro,Cornwall,Tr1 3lj,United Kingdom

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Nottingham,Ng5 1pb,United Kingdom

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Birmingham,B15 2th,United Kingdom

Community Cancer Trials of Utah

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Ogden,Utah,84405,United States

Sibian Torres
Carl Gray

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Bethesda,Maryland,20817,United States

Natalie Bongiorno
Ralph V Boccia

Clinical Research Alliance Research

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Lake Success,New York,11042,United States

William Krenn
James D Olimpio

Texas Oncology-Baylor Res Ins

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Dallas,Texas,75204,United States

Dominique Marquez
Moshe Yair Levy

University of Colorado Anschutz

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Aurora,Colorado,80045,United States

George Gemlyn

St Vincent Frontier Cancer Center .

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Billings,Montana,59102,United States

Patrick Cobb
Amanda Klein

INTEGRIS Cancer Institute of Oklahoma Integris South West Med Center

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Oklahoma City,Oklahoma,73142,United States

Basgar Alasad
Kellie Larsen-Dyer

Yuma Regional Medical Center

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Yuma,Arizona,85349,United States

Abhinav Chandra
Amy Olmeda

Hematology Oncology Association of Rockland

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Nyack,New York,10960,United States

Marion VanWoudenberg
Sung Ho Lee

Summit Health

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Florham Park,New Jersey,07932,United States

David Gallinson

Michigan Center of Medical Research

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Farmington Hills,Michigan,48334,United States

Faisal Musa

Texas Oncology

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McAllen,Texas,78503,United States

Louise Philipp
Nurul Wahid

Napa Research

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Margate,Florida,33063,United States

Emilio Araujo-Mino

Community Cancer Institute

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Clovis,California,93611,United States

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Mohammed Bukari

University of Pennsylvania

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Philadelphia,Pennsylvania,19104,United States

Adam Cuker
Emmanuel Ndukwudimma

Mayo Clinic Rochester Mayo Clinic Rochester

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Rochester,Minnesota,55905,United States

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Cleveland Clinic Foundation .

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Cleveland,Ohio,44195,United States

Alan Lichtin
Antonio Wilson

Uni of Chi Medi Ctr Hema and Onco Main Centre

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Chicago,Illinois,60637,United States

Michael Drazer
Sara Moellering

Inspira Medical Cent Mullica Hill

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Mullica Hill,New Jersey,08062,United States

Catherine Vasquez
Erev Tubb

Mays Cancer Ctr Uthsa Mdacc UTHSCSA

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San Antonio,Texas,78229,United States

Elizabeth Bowhay-Carnes

Compassionate Care Res Group Inc

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Fountain Valley,California,92708,United States

Eric Lee

Rhode Island Hospital

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Providence,Rhode Island,02903,United States

Andrew Hsu

Metro Minnesota CCOP Main Site Address Oncology

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Saint Louis Park,Minnesota,55416,United States

Yan Ji

STAT Research Inc Premier Clin Res LLC STAT Res

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Dayton,Ohio,45402,United States

Aby Madrigal
Charles Bane

Parkview Research Center .

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Fort Wayne,Indiana,46845,United States

Jeffrey Letzer

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Hanoi,100000,Vietnam

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Ho Chi Minh,738000,Vietnam

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