Last Update: Oct 01, 2024
An Open-label, Single Arm, Multicenter Extension Study to Evaluate Long-term Safety and Tolerability of Inclisiran in Participants With Heterozygous or Homozygous Familial Hypercholesterolemia Who Have Completed the Adolescent ORION-16 or ORION-13 Studies (VICTORION-PEDS-OLE)
ClinicalTrials.gov Identifier:
Novartis Reference Number:CKJX839C12001B
All compounds are either investigational or being studied for (a) new use(s). Efficacy and safety have not been established. There is no guarantee that they will become commercially available for the use(s) under investigation.

Study Description

The purpose of this open-label, single arm, multicenter extension study is to evaluate the long-term safety and tolerability of inclisiran in participants with HeFH or HoFH who have completed the ORION-16 or ORION-13 studies. This is an open-label, single arm, multicenter study designed to evaluate long-term safety and tolerability of inclisiran. In addition, the study will provide participants the opportunity to have continued access to treatment with inclisiran.

Heterozygous or Homozygous Familial Hypercholesterolemia
Phase3
Recruiting
154
Feb 10, 2023
Jun 30, 2028
All
12 Years - (Child, Adult, Older Adult)

Interventions

Drug

Inclisiran

Inclisiran sodium 300mg (equivalent to 284mg inclisiran\*) in 1.5mL solution administered subcutaneously in pre-filled syringe

Eligibility Criteria

Key inclusion:

* Male and female participants with a diagnosis of HeFH or HoFH who completed the ORION-16 or ORION-13 studies
* Per investigator's clinical judgment, participant derived benefit from treatment with inclisiran in the ORION-16 or ORION-13 studies

Key exclusion:

* Participants who in the feeder inclisiran ORION-16 and ORION-13 studies either screen failed or permanently discontinued from the treatment/study for any reason or had serious safety or tolerability issues related to inclisiran treatment
* Any uncontrolled or serious disease, or any medical, physical, or surgical condition, that may either interfere with participation in the clinical study or interpretation of clinical study results, and/or put the participant at significant risk

Novartis Investigative Site

Recruiting

Fortaleza,Ceara,60430275,Brazil

Novartis Investigative Site

Recruiting

Sao Paulo,SP,04023-900,Brazil

Novartis Investigative Site

Recruiting

Sao Paulo,SP,05403 000,Brazil

Novartis Investigative Site

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Toulouse Cedex,31059,France

Novartis Investigative Site

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Athens,115 27,Greece

Novartis Investigative Site

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Jerusalem,9112001,Israel

Novartis Investigative Site

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Ramat Gan,52621,Israel

Novartis Investigative Site

Recruiting

Modena,MO,41124,Italy

Novartis Investigative Site

Recruiting

Roma,RM,00165,Italy

Novartis Investigative Site

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Ashrafieh,166830,Lebanon

Novartis Investigative Site

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Rotterdam,Zuid Holland,3015 gd,Netherlands

Novartis Investigative Site

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Amsterdam,1105 az,Netherlands

Novartis Investigative Site

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Oslo,0514,Norway

Novartis Investigative Site

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Gdansk,80 952,Poland

Novartis Investigative Site

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Ljubljana,1000,Slovenia

Novartis Investigative Site

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Bloemfontein,Free State,9301,South Africa

Novartis Investigative Site

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Cape Town,Western Cape,7130,South Africa

Novartis Investigative Site

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Oviedo,Asturias,33011,Spain

Novartis Investigative Site

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Pamplona,Navarra,31008,Spain

Novartis Investigative Site

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A Coruna,15001,Spain

Novartis Investigative Site

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Cordoba,Andalucia,14004,Spain

Novartis Investigative Site

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Geneve 14,1211,Switzerland

Novartis Investigative Site

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Adana,01330,Turkey

Novartis Investigative Site

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Ankara,06500,Turkey

Novartis Investigative Site

Recruiting

Middlesex,Ub9 6jh,United Kingdom

Cincinnati Childrens Hospital MC .

Recruiting

Cincinnati,Ohio,45229-3039,United States

Bliss Magella
Amy Shah

Excel Medical Clinical Trials LLC

Recruiting

Boca Raton,Florida,33434,United States

Emilio Vega
Seth J Baum

Worldwide Contacts

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Novartis Pharmaceuticals

Novartis Pharmaceuticals