Last Update: Nov 25, 2024
A Phase III, Randomized, Double-blind Study of Ianalumab (VAY736) Versus Placebo in Addition to First-line Corticosteroids in Primary Immune Thrombocytopenia (VAYHIT1)
ClinicalTrials.gov Identifier:
Novartis Reference Number:CVAY736I12301
All compounds are either investigational or being studied for (a) new use(s). Efficacy and safety have not been established. There is no guarantee that they will become commercially available for the use(s) under investigation.

Study Description

The purpose of this study is to evaluate the effect of two different doses of ianalumab versus placebo in addition to first-line corticosteroids in maintaining platelet count ≥30 G/L in adult participants with primary ITP. This is a multi-center, randomized, double-blind Phase 3 study to assess the efficacy and safety of two different doses of ianalumab compared to placebo in adults with primary ITP (platelets count \<30 G/L) who require first-line standard-of-care corticosteroids.

After completion of the screening period, the participants will enter the randomized treatment period (ianalumab/placebo with standard of care corticosteroids).

After the treatment period, all participants will enter the follow-up period to be monitored for efficacy and safety or safety only depending on how they respond to the study treatment.

Primary Immune Thrombocytopenia (ITP)
Phase3
Recruiting
225
Mar 06, 2023
Dec 18, 2028
All
18 Years - (Adult, Older Adult)

Interventions

Drug

Corticosteroids

Oral or parental (if clinically justified)
Biological

Ianalumab

Intravenous infusion, prepared from concentrate solution
Drug

Placebo

Intravenous infusion, prepared from matching placebo

Eligibility Criteria

Inclusion Criteria:

* Signed informed consent prior to participation in the study.
* Male or female participants aged 18 years and older on the day of signing informed consent
* Primary ITP diagnosed within 3 months before initiating first-line ITP therapy (corticosteroids, IVIG)
* Platelet count below 30 G/L before starting any first-line ITP therapy (corticosteroids, IVIG)
* Response (platelet count \>=50 G/L) to corticosteroids (+/- IVIG) at any time prior to randomization. Note: Platelet count measured within 7 days of platelet transfusion will not be considered as response.

Key Exclusion Criteria:

* Evans syndrome or any other cytopenia (patients with anemia related to bleeding or iron deficiency are eligible)
* Current life-threatening bleeding
* Previous ITP treatment, including splenectomy, except for corticosteroids and/or IVIG initiated as first-line therapy for up to 28 days before randomization and rescue corticosteroids and/or IVIG given prior to confirmed diagnosis of primary ITP .
* Prior use of B-cell depleting therapy (e.g., rituximab).
* Absolute neutrophil count below 1.0 G/L at randomization
* Participants with concurrent coagulation disorders and/or receiving anti-platelet or anticoagulant medication with an exemption of low dose of acetylsalicylic acid

Other protocol-defined Inclusion/Exclusion may apply.

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Ciudad Autonoma de Bs As,Buenos Aires,C1015abo,Argentina

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Tucuman,San Miguel De Tucuman,4000,Argentina

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Buenos aires,C1039aac,Argentina

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Cordoba,5000,Argentina

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Caba,Buenos Aires,C1280aeb,Argentina

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Caba,Buenos Aires,C1414drk,Argentina

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Clayton,Victoria,3168,Australia

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Melbourne,Victoria,3004,Australia

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Canberra,Australian Capital Territory,2605,Australia

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Wooloongabba,Queensland,4102,Australia

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Innsbruck,Tyrol,6020,Austria

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Salzburg,5020,Austria

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Wien,1140,Austria

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Brugge,8000,Belgium

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Leuven,3000,Belgium

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Roeselare,8800,Belgium

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Brasschaat,2930,Belgium

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Plovdiv,4002,Bulgaria

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Sofia,1413,Bulgaria

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Sofia,1431,Bulgaria

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Varna,9010,Bulgaria

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Wuhan,Hubei,430022,China

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Jinan,250012,China

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Beijing,Beijing,100044,China

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Chengdu,Sichuan,610041,China

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Changsha,Hunan,410008,China

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Shijiazhuang,050000,China

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Chongqing,Chongqing,400010,China

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Kunming,Yunnan,650101,China

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Tianjin,300020,China

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Guangzhou,Guangdong,510515,China

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Hangzhou,Zhejiang,310003,China

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Changzhou,Jiangsu,213004,China

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Shenzhen,Guangdong,518037,China

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Hangzhou,Zhejiang,310006,China

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Nanchang,Jiangxi,330006,China

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Luoyang,Henan,471003,China

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Bengbu,233004,China

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Xian,Shaanxi,710004,China

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Zhengzhou,Henan,450052,China

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Dalian,116000,China

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Taiyuan,Shanxi,030001,China

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Praha,12808,Czechia

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Ostrava,Poruba,708 52,Czechia

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Brno Bohunice,625 00,Czechia

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Praha 10,100 34,Czechia

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Caen,14033,France

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Chambery cedex,73011,France

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Le Mans,72000,France

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Lille,59037,France

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Paris,75014,France

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Rennes,35043,France

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Dresden,01307,Germany

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Essen,45147,Germany

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Frankfurt,60590,Germany

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Giessen,35392,Germany

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Hannover,30161,Germany

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Jena,07740,Germany

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New Territories,Hong Kong

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Budapest,H-1083,Hungary

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Debrecen,4032,Hungary

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Ahmedabad,Gujarat,380013,India

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Mumbai,Maharashtra,400012,India

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Kolkata,West Bengal,700094,India

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Bologna,BO,40138,Italy

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Firenze,FI,50134,Italy

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Roma,RM,00168,Italy

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Trieste,TS,34129,Italy

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Vicenza,VI,36100,Italy

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Iruma-gun,Saitama,350-0495,Japan

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Gifu shi,Gifu,500 8513,Japan

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Chiba,260-0852,Japan

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Shibukawa-city,Gunma,377-0280,Japan

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Fukuoka,815-8555,Japan

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Sapporo,Hokkaido,060-8604,Japan

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Matsumoto-city,Nagano,399-8701,Japan

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Okayama city,Okayama,701-1192,Japan

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Osaka-city,Osaka,543-8555,Japan

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Nagakute-city,Aichi,480-1195,Japan

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Selangor,68000,Malaysia

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Kuching,Sarawak,93586,Malaysia

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Johor Bahru,80100,Malaysia

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Kuala Lumpur,56000,Malaysia

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Penang,10050,Malaysia

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Ciudad De Mexico,Mexico CP,14080,Mexico

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Morelia,Michoacan,58260,Mexico

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Monterrey,Nuevo Leon,64460,Mexico

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Gralum,1714,Norway

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Bucharest,030171,Romania

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Bucuresti,013975,Romania

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Bucharest,District 2,022328,Romania

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Singapore,119074,Singapore

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Singapore,169608,Singapore

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Singapore,S308433,Singapore

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Salamanca,Castilla Y Leon,37007,Spain

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Barcelona,Catalunya,08035,Spain

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Madrid,28009,Spain

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Madrid,28046,Spain

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Murcia,30008,Spain

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Sevilla,Andalucia,41013,Spain

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Chiang Mai,50200,Thailand

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Bangkok,10330,Thailand

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Bangkok,10700,Thailand

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Samsun,55139,Turkey

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Istanbul,TUR,34098,Turkey

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Aydin,09100,Turkey

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Edirne,22030,Turkey

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Istanbul,34214,Turkey

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Izmir,35100,Turkey

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London,W12 0hs,United Kingdom

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Truro,Cornwall,Tr1 3lj,United Kingdom

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Nottingham,Ng5 1pb,United Kingdom

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Birmingham,B15 2th,United Kingdom

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Southampton,So16 6yd,United Kingdom

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Glasgow,G31 2er,United Kingdom

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Leeds,Ls1 3ex,United Kingdom

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Liverpool,L7 8xp,United Kingdom

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London,Sw17 0qt,United Kingdom

St Vincent Frontier Cancer Center

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Billings,Montana,59102,United States

Patrick Cobb
Amanda Klein

Oncology Care Associates

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Bethesda,Maryland,20817,United States

Ralph V Boccia
Natalie Bongiorno

Texas Oncology-Baylor Res Ins

Recruiting

Dallas,Texas,75204,United States

Moshe Yair Levy
Dominique Marquez

Uni of Chi Medi Ctr Hema and Onco

Recruiting

Chicago,Illinois,60637,United States

Sara Moellering
Michael Drazer

Compassionate Care Res Group Inc

Recruiting

Fountain Valley,California,92708,United States

Eric Lee

INTEGRIS Cancer Institute of Oklahoma

Recruiting

Oklahoma City,Oklahoma,73142,United States

Basgar Alasad
Kellie Larsen-Dyer

Hematology Oncology Association of Rockland

Recruiting

Nyack,New York,10960,United States

Sung Ho Lee
Marion VanWoudenberg

Clinical Research Alliance

Recruiting

Lake Success,New York,11042,United States

James D Olimpio
William Krenn

Michigan Center of Medical Research

Recruiting

Farmington Hills,Michigan,48334,United States

Faisal Musa

Texas Oncology

Recruiting

McAllen,Texas,78503,United States

Nereida Salinas
Nurul Wahid

Parkview Research Center

Recruiting

Fort Wayne,Indiana,46845,United States

Jeffrey Letzer

University of Pennsylvania

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Philadelphia,Pennsylvania,19104,United States

Adam Cuker
Emmanuel Ndukwudimma

Summit Health

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Florham Park,New Jersey,07932,United States

David Gallinson

University of Colorado Anschutz

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Aurora,Colorado,80045,United States

George Gemlyn

Mayo Clinic Rochester

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Rochester,Minnesota,55905,United States

Alexandra Wolanskyj

Mays Cancer Ctr Uthsa Mdacc

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San Antonio,Texas,78229,United States

Elizabeth Bowhay-Carnes

Yuma Regional Medical Center

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Yuma,Arizona,85349,United States

Abhinav Chandra
Amy Olmeda

Cleveland Clinic Foundation

Recruiting

Cleveland,Ohio,44195,United States

Alan Lichtin
Kyle Shepherd

Community Cancer Trials of Utah

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Ogden,Utah,84405,United States

Carl Gray
Jenny Flores

Rhode Island Hospital

Recruiting

Providence,Rhode Island,02903,United States

Andrew Hsu

Inspira Medical Cent Mullica Hill

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Mullica Hill,New Jersey,08062,United States

Catherine Vasquez
Erev Tubb

Metro Minnesota CCOP

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Saint Louis Park,Minnesota,55416,United States

Yan Ji

Napa Research

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Margate,Florida,33063,United States

Emilio Araujo-Mino

Community Cancer Institute

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Clovis,California,93611,United States

Kelly Meehan
Mohammed Bukari

STAT Research Inc

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Dayton,Ohio,45402,United States

Charles Bane
Kyle Tipton

Novartis Investigative Site

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Hanoi,100000,Vietnam

Novartis Investigative Site

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Ho Chi Minh,738000,Vietnam

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