Last Update: Oct 23, 2024
A Phase 3 Randomized, Double-blind Study of Ianalumab (VAY736) Versus Placebo in Addition to Eltrombopag in Patients With Primary Immune Thrombocytopenia (ITP) Who Had an Insufficient Response or Relapsed After First Line Steroid Treatment (VAYHIT2)
ClinicalTrials.gov Identifier:
Novartis Reference Number:CVAY736Q12301
All compounds are either investigational or being studied for (a) new use(s). Efficacy and safety have not been established. There is no guarantee that they will become commercially available for the use(s) under investigation.

Study Description

The purpose of this study is to evaluate the effect of two different doses of ianalumab
added to eltrombopag to prolong Time to Treatment Failure (TTF) in adults with primary
ITP who failed previous first-line treatment with steroids. This is a multicenter, randomized, double-blinded phase 3 study to assess efficacy and
safety of two different doses of ianalumab versus placebo in addition to eltrombopag in
adults with primary ITP (platelet count <30 G/L) who failed previous first-line treatment
with corticosteroids.

After completion of the screening period, the participants will enter the randomized
treatment period (ianalumab/placebo with eltrombopag) followed by the eltrombopag
tapering period. Afterwards, all participants will enter the follow-up period to be
monitored for efficacy and safety or safety only depending on how the participants
responded to the study treatment.

Primary Immune Thrombocytopenia
Phase3
Recruiting
150
Feb 02, 2023
May 19, 2028
All
18 Years - (Adult, Older Adult)

Interventions

Drug

Eltrombopag

Film-coated tablet for oral use
Biological

Ianalumab

Concentrate for solution for infusion for intravenous use
Drug

Placebo

Concentrate for solution for infusion for intravenous use.

Eligibility Criteria

Key Inclusion criteria

1. Male or female patients aged 18 years and older on the day of signing the informed
consent.

2. A signed informed consent must be obtained prior to participation in the study.

3. A diagnosis of primary ITP, with insufficient response to, or relapse after a
first-line corticosteroid therapy ± IVIG.

4. Patient with platelet count <30G/L (whom eltrombopag is clinically indicated as per
physician's discretion) and with no contraindication to receive eltrombopag

Key Exclusion criteria

1. ITP patients who received second-line ITP treatments (other than steroid therapy±
IVIG) including splenectomy. However, patients exposed to thrombopoietin receptor
agonists (TPO-RAs) for a limited time (max one week) before screening are eligible.

2. Patients with key lab abnormalities and patients with Evans syndrome or any other
cytopenia, (patients with low grade anemia related to bleeding or iron deficiency
are eligible).

3. Patients with history of clinically significant hematological disorders, or with
marked altered hematologic parameters

4. Patients with current or history of life-threatening bleeding

5. Patient that are Human Immunodeficiency Virus (HIV), Hepatitis C Virus (HCV),
Hepatitis B surface Antigen (HBsAg)/ Hepatitis B core antibody (HBcAb)-positive.
HBcAb-positive patients can be enrolled if HBsAg negative, HBV DNA negative, no
pre-existing liver fibrosis is present and antiviral prophylaxis is given

6. Patients with known active or uncontrolled infection requiring systemic treatment
during screening period

7. Patients with hepatic impairment

8. Patients with concurrent coagulation disorders and/or receiving antiplatelet or
anticoagulant medication with an exemption of low dose of acetylsalicylic acid (≤150
mg daily)

9. Nursing (breast feeding) or pregnant women

Other protocol-defined inclusion/exclusion criteria may apply.

Novartis Investigative Site

Recruiting

Caba,Buenos Aires,C1181ach,Argentina

Novartis Investigative Site

Recruiting

Buenos Aires,C1425aum,Argentina

Novartis Investigative Site

Recruiting

Clayton,Victoria,3168,Australia

Novartis Investigative Site

Recruiting

Parkville,Victoria,3050,Australia

Novartis Investigative Site

Recruiting

Linz,4010,Austria

Novartis Investigative Site

Recruiting

Vienna,A 1090,Austria

Novartis Investigative Site

Recruiting

Wels,A 4600,Austria

Novartis Investigative Site

Recruiting

Brugge,8000,Belgium

Novartis Investigative Site

Recruiting

Leuven,3000,Belgium

Novartis Investigative Site

Recruiting

Roeselare,8800,Belgium

Novartis Investigative Site

Recruiting

Yvoir,5530,Belgium

Novartis Investigative Site

Recruiting

Jinan,250012,China

Novartis Investigative Site

Recruiting

Wuhan,Hubei,430022,China

Novartis Investigative Site

Recruiting

Tianjin,300020,China

Novartis Investigative Site

Recruiting

Suzhou,Jiangsu,215006,China

Novartis Investigative Site

Recruiting

Tianjin,300052,China

Novartis Investigative Site

Recruiting

Binzhou,Shandong,256603,China

Novartis Investigative Site

Recruiting

Hangzhou,Zhejiang,310003,China

Novartis Investigative Site

Recruiting

Beijing,Beijing,100044,China

Novartis Investigative Site

Recruiting

Beijing,100730,China

Novartis Investigative Site

Recruiting

Guangzhou,Guangdong,510515,China

Novartis Investigative Site

Recruiting

Brno Bohunice,625 00,Czechia

Novartis Investigative Site

Recruiting

Praha 10,100 34,Czechia

Novartis Investigative Site

Recruiting

Praha,12808,Czechia

Novartis Investigative Site

Recruiting

Le Mans,72000,France

Novartis Investigative Site

Recruiting

Vandoeuvre Les Nancy,54511,France

Novartis Investigative Site

Recruiting

Blois Cedex,41000,France

Novartis Investigative Site

Recruiting

Koeln,50937,Germany

Novartis Investigative Site

Recruiting

Dresden,01307,Germany

Novartis Investigative Site

Recruiting

Giessen,35392,Germany

Novartis Investigative Site

Recruiting

Hannover,30161,Germany

Novartis Investigative Site

Recruiting

Jena,07740,Germany

Novartis Investigative Site

Recruiting

Budapest,H-1083,Hungary

Novartis Investigative Site

Recruiting

Debrecen,4032,Hungary

Novartis Investigative Site

Recruiting

Rishikesh,Uttarakhand,249203,India

Novartis Investigative Site

Recruiting

Kolkata,West Bengal,700014,India

Novartis Investigative Site

Recruiting

Chandigarh,160 012,India

Novartis Investigative Site

Recruiting

Roma,RM,00133,Italy

Novartis Investigative Site

Recruiting

Roma,RM,00168,Italy

Novartis Investigative Site

Recruiting

Torino,TO,10126,Italy

Novartis Investigative Site

Recruiting

Trieste,TS,34129,Italy

Novartis Investigative Site

Recruiting

Vicenza,VI,36100,Italy

Novartis Investigative Site

Recruiting

Bologna,BO,40138,Italy

Novartis Investigative Site

Recruiting

Bunkyo-ku,Tokyo,113-8603,Japan

Novartis Investigative Site

Recruiting

Narita,Chiba,286-8523,Japan

Novartis Investigative Site

Recruiting

Chiyoda-ku,Tokyo,101-8643,Japan

Novartis Investigative Site

Recruiting

Kumamoto-city,Kumamoto,860-0008,Japan

Novartis Investigative Site

Recruiting

Chuo ku,Tokyo,104 8560,Japan

Novartis Investigative Site

Recruiting

Omura,Nagasaki,856-8562,Japan

Novartis Investigative Site

Recruiting

Kofu-city,Yamanashi,400-8506,Japan

Novartis Investigative Site

Recruiting

Hirakata-city,Osaka,573-1191,Japan

Novartis Investigative Site

Recruiting

Aomori,030 8553,Japan

Novartis Investigative Site

Recruiting

Osaka-city,Osaka,540-0006,Japan

Novartis Investigative Site

Recruiting

Hiroshima,730-8619,Japan

Novartis Investigative Site

Recruiting

Suita,Osaka,565 0871,Japan

Novartis Investigative Site

Recruiting

Nagoya,Aichi,453-8511,Japan

Novartis Investigative Site

Recruiting

Jeollanam,519763,Korea, Republic of

Novartis Investigative Site

Recruiting

Seoul,06351,Korea, Republic of

Novartis Investigative Site

Recruiting

Seoul,158-710,Korea, Republic of

Novartis Investigative Site

Recruiting

Seoul,Seocho Gu,06591,Korea, Republic of

Novartis Investigative Site

Recruiting

Johor Bahru,80100,Malaysia

Novartis Investigative Site

Recruiting

Kuala Lumpur,56000,Malaysia

Novartis Investigative Site

Recruiting

Penang,10050,Malaysia

Novartis Investigative Site

Recruiting

Pulau Pinang,10990,Malaysia

Novartis Investigative Site

Recruiting

Kota Kinabalu,Sabah,88586,Malaysia

Novartis Investigative Site

Recruiting

Selangor,68000,Malaysia

Novartis Investigative Site

Recruiting

Kuching,Sarawak,93586,Malaysia

Novartis Investigative Site

Recruiting

Subang Jaya,Selangor,47500,Malaysia

Novartis Investigative Site

Recruiting

Monterrey,Nuevo Leon,64460,Mexico

Novartis Investigative Site

Recruiting

Ciudad De Mexico,Mexico CP,14080,Mexico

Novartis Investigative Site

Recruiting

Morelia,Michoacan,58260,Mexico

Novartis Investigative Site

Recruiting

Leiden,Zuid Holland,2333 za,Netherlands

Novartis Investigative Site

Recruiting

Utrecht,3584cx,Netherlands

Novartis Investigative Site

Recruiting

Gralum,1714,Norway

Novartis Investigative Site

Recruiting

Quezon,1102,Philippines

Novartis Investigative Site

Recruiting

Makati City,1229,Philippines

Novartis Investigative Site

Recruiting

Bucharest,District 2,022328,Romania

Novartis Investigative Site

Recruiting

Bucharest,030 171,Romania

Novartis Investigative Site

Recruiting

Craiova,200136,Romania

Novartis Investigative Site

Recruiting

Sibiu,550245,Romania

Novartis Investigative Site

Recruiting

Timisoara,300079,Romania

Novartis Investigative Site

Recruiting

Singapore,119074,Singapore

Novartis Investigative Site

Recruiting

Singapore,169608,Singapore

Novartis Investigative Site

Recruiting

Singapore,S308433,Singapore

Novartis Investigative Site

Recruiting

Madrid,28046,Spain

Novartis Investigative Site

Recruiting

Murcia,30008,Spain

Novartis Investigative Site

Recruiting

Salamanca,Castilla Y Leon,37007,Spain

Novartis Investigative Site

Recruiting

Barcelona,Catalunya,08003,Spain

Novartis Investigative Site

Recruiting

Santiago De Compostela,Galicia,15706,Spain

Novartis Investigative Site

Recruiting

Madrid,28041,Spain

Novartis Investigative Site

Recruiting

Kaohsiung,83301,Taiwan

Novartis Investigative Site

Recruiting

Taoyuan,33305,Taiwan

Novartis Investigative Site

Recruiting

Chiang Mai,50200,Thailand

Novartis Investigative Site

Recruiting

Bangkok,10330,Thailand

Novartis Investigative Site

Recruiting

Bangkok,10700,Thailand

Novartis Investigative Site

Recruiting

Istanbul,TUR,34098,Turkey

Novartis Investigative Site

Recruiting

Ankara,06100,Turkey

Novartis Investigative Site

Recruiting

Aydin,09100,Turkey

Novartis Investigative Site

Recruiting

Edirne,22030,Turkey

Novartis Investigative Site

Recruiting

Izmir,35100,Turkey

Novartis Investigative Site

Recruiting

Samsun,55139,Turkey

Novartis Investigative Site

Recruiting

Southampton,So16 6yd,United Kingdom

Novartis Investigative Site

Recruiting

Truro,Cornwall,Tr1 3lj,United Kingdom

Novartis Investigative Site

Recruiting

London,E1 1bb,United Kingdom

Novartis Investigative Site

Recruiting

London,Sw17 0qt,United Kingdom

Novartis Investigative Site

Recruiting

London,W12 0hs,United Kingdom

Novartis Investigative Site

Recruiting

Nottingham,Ng5 1pb,United Kingdom

Novartis Investigative Site

Recruiting

Oxford,Ox3 7le,United Kingdom

Hematology Oncology Association of Rockland

Recruiting

Nyack,New York,10960,United States

Marion VanWoudenberg
Sung Ho Lee

Uni of Chi Medi Ctr Hema and Onco Main Centre

Recruiting

Chicago,Illinois,60637,United States

Michael Drazer
Sara Moellering

Summit Health

Recruiting

Florham Park,New Jersey,07932,United States

David Gallinson

Community Cancer Institute

Recruiting

Clovis,California,93611,United States

Mohammed Bukari

Texas Oncology Drug Ship 5

Recruiting

Dallas,Texas,75251,United States

Racha Halawi

UMASS Memorial Medical Center

Recruiting

Worcester,Massachusetts,01665,United States

Daniel Winokur
Lindsey Allen

Compassionate Care Res Group Inc

Recruiting

Fountain Valley,California,92708,United States

Eric Lee

STAT Research Inc Premier Clin Res LLC STAT Res

Recruiting

Dayton,Ohio,45402,United States

Charles Bane

NorthShore University Health System

Recruiting

Evanston,Illinois,60201,United States

Amy Wang
Michele Britto

Montefiore Medical Center .

Recruiting

Bronx,New York,10461,United States

Irina Murakhovskaya
Noelle Townsend

Center of Clnl Rsch and Innovation

Recruiting

Houston,Texas,77008,United States

Adriana Mccray
John Knecht

Michigan Center of Medical Research

Recruiting

Farmington Hills,Michigan,48334,United States

Faisal Musa

INTEGRIS Cancer Institute of Oklahoma Integris South West Med Center

Recruiting

Oklahoma City,Oklahoma,73142,United States

Basgar Alasad
Kellie Larsen-Dyer

University of Colorado Anschutz

Recruiting

Aurora,Colorado,80045,United States

George Gemlyn

Washington U Sch Of Med Ctr For CS Center For Advanced Medicine

Recruiting

Saint Louis,Missouri,63110,United States

Morey A. Blinder

Yuma Regional Medical Center

Recruiting

Yuma,Arizona,85349,United States

Abhinav Chandra
Amy Olmeda

Parkview Research Center .

Recruiting

Fort Wayne,Indiana,46845,United States

Jeffrey Letzer

Clinical Research Alliance Research

Recruiting

Lake Success,New York,11042,United States

James D Olimpio
William Krenn

Community Cancer Trials of Utah

Recruiting

Ogden,Utah,84405,United States

Carl Gray
Sibian Torres

St Vincent Frontier Cancer Center .

Recruiting

Billings,Montana,59102,United States

Amanda Klein
Patrick Cobb

University of Pennsylvania

Recruiting

Philadelphia,Pennsylvania,19104,United States

Adam Cuker
Emmanuel Ndukwudimma

Boston Medical Center

Recruiting

Boston,Massachusetts,02118,United States

J Mark Sloan

Napa Research

Recruiting

Margate,Florida,33063,United States

Emilio Araujo-Mino

Worldwide Contacts

If the location of your choosing does not feature any contact detail, please reach out using the information below.

Novartis Pharmaceuticals

Novartis Pharmaceuticals