Active Clinical Trials

Clinical trials are at the heart of our work to bring innovative medicines to people with a particular disease or condition. Learn more about the active studies conducted by Novartis including opportunities to get involved.

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Study title Condition Phase Location

Rollover Study for Patients With Sickle Cell Disease Who Have Completed a Prior Novartis-Sponsored Crizanlizumab Study

Sickle Cell Disease Phase4 United States
Turkey
Lebanon
Belgium
Colombia
Germany
Spain
Oman
Italy
France
Brazil
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CAR-T Long Term Follow Up (LTFU) Study

Long Term Safety of Patients Receiving CAR-T in an Eligible Clinical Trial or Managed Access Program Phase3 United States
Spain
Germany
Australia
Japan
Denmark
Belgium
Canada
Finland
United Kingdom
Italy
Norway
France
Israel
Singapore
Taiwan
Austria
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A 24-week rPMS Study in Real-world Setting for Enerzair

Asthma Korea, Republic of

Asciminib RMP Study

Chronic Myeloid Leukemia Korea, Republic of

Asciminib Roll-over Study

Chronic Myelogenous Leukemia, Leukemia, Myelogenous, Chronic, BCR-ABL Positive Phase4 United States
Spain
Germany
France
Czechia
Argentina
Denmark
Portugal
Italy
Mexico
Canada
Russian Federation
United Kingdom
Brazil
Turkey
Romania
Bulgaria
Poland
Austria
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Ofatumumab in Portuguese Multiple Sclerosis Patients - an Observational Study

Relapsing Multiple Sclerosis Portugal

Safety and Efficacy of Fingolimod in Pediatric Patients With Multiple Sclerosis

Multiple Sclerosis Phase3 Serbia
Ukraine
United Kingdom
Spain
France
United States
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Study of Efficacy and Safety of Iptacopan in Participants With IC-MPGN

IC-MPGN Phase3 United States
Turkey
Spain
Italy
United Kingdom
Brazil
Germany
Switzerland
Argentina
Japan
Israel
Vietnam
France
Canada
India
Poland
Czechia
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Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

Spinal Muscular Atrophy (SMA) United States
Russian Federation
Japan
Portugal
Ireland
Greece
Taiwan
Korea, Republic of
Israel
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A NIS of Alpelisib in Combination With Fulvestrant in Postmenopausal Women, and Men, With HR+,HER2- , Locally Advanced or Metastatic Breast Cancer With a PIK3CA Mutation, After Disease Progression Following Endocrine Therapy as Monotherapy, in the Real-world Setting

Hormone Receptor Positive HER2 Negative Breast Cancer With a PIK3CA Mutation Spain
Italy